Molecular Therapy-Methods & Clinical Development

Papers
(The TQCC of Molecular Therapy-Methods & Clinical Development is 14. The table below lists those papers that are above that threshold based on CrossRef citation counts [max. 250 papers]. The publications cover those that have been published in the past four years, i.e., from 2020-02-01 to 2024-02-01.)
ArticleCitations
Airways Expression of SARS-CoV-2 Receptor, ACE2, and TMPRSS2 Is Lower in Children Than Adults and Increases with Smoking and COPD216
Oncolytic Viruses and the Immune System: The Dynamic Duo145
Barriers and Strategies of Cationic Liposomes for Cancer Gene Therapy109
The Two Faces of ACE2: The Role of ACE2 Receptor and Its Polymorphisms in Hypertension and COVID-19105
Optimizing CAR-T Cell Manufacturing Processes during Pivotal Clinical Trials85
Analytical methods for process and product characterization of recombinant adeno-associated virus-based gene therapies77
Methods Matter: Standard Production Platforms for Recombinant AAV Produce Chemically and Functionally Distinct Vectors77
Adeno-Associated Viral Vectors in Neuroscience Research71
CNS Transduction Benefits of AAV-PHP.eB over AAV9 Are Dependent on Administration Route and Mouse Strain70
Suprachoroidal and Subretinal Injections of AAV Using Transscleral Microneedles for Retinal Gene Delivery in Nonhuman Primates69
Synthetic mRNA Encoding VEGF-A in Patients Undergoing Coronary Artery Bypass Grafting: Design of a Phase 2a Clinical Trial68
Rapid evolution of blood-brain-barrier-penetrating AAV capsids by RNA-driven biopanning66
Ready for Repair? Gene Editing Enters the Clinic for the Treatment of Human Disease64
Circular RNAs: Promising Molecular Biomarkers of Human Aging-Related Diseases via Functioning as an miRNA Sponge64
Intramuscular Delivery of Replicon RNA Encoding ZIKV-117 Human Monoclonal Antibody Protects against Zika Virus Infection61
CRISPR-Cas9 gene editing of hepatitis B virus in chronically infected humanized mice60
Production of Lentiviral Vectors Using Suspension Cells Grown in Serum-free Media56
Immune Response Mechanisms against AAV Vectors in Animal Models55
AAV-Mediated CRISPR/Cas9 Gene Editing in Murine Phenylketonuria54
Use of Nanovesicles from Orange Juice to Reverse Diet-Induced Gut Modifications in Diet-Induced Obese Mice54
Therapeutic Mesenchymal Stromal Cells for Immunotherapy and for Gene and Drug Delivery54
Genome Editing in Patient iPSCs Corrects the Most Prevalent USH2A Mutations and Reveals Intriguing Mutant mRNA Expression Profiles51
Preclinical Toxicology of rQNestin34.5v.2: An Oncolytic Herpes Virus with Transcriptional Regulation of the ICP34.5 Neurovirulence Gene50
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?49
Comparison of analytical techniques to quantitate the capsid content of adeno-associated viral vectors48
Successful Transduction with AAV Vectors after Selective Depletion of Anti-AAV Antibodies by Immunoadsorption47
Increasing CRISPR Efficiency and Measuring Its Specificity in HSPCs Using a Clinically Relevant System45
A High-Throughput Method for Characterizing Novel Chimeric Antigen Receptors in Jurkat Cells43
Creation of a High-Yield AAV Vector Production Platform in Suspension Cells Using a Design-of-Experiment Approach42
Digital PCR Assays for Precise Quantification of CD19-CAR-T Cells after Treatment with Axicabtagene Ciloleucel42
Acerola exosome-like nanovesicles to systemically deliver nucleic acid medicine via oral administration42
Enhanced expression of immune checkpoint receptors during SARS-CoV-2 viral infection40
Development of Large-Scale Downstream Processing for Lentiviral Vectors39
qPCR and qRT-PCR analysis: Regulatory points to consider when conducting biodistribution and vector shedding studies39
Preclinical Evaluation of a Novel Lentiviral Vector Driving Lineage-Specific BCL11A Knockdown for Sickle Cell Gene Therapy38
High Levels of Frataxin Overexpression Lead to Mitochondrial and Cardiac Toxicity in Mouse Models38
AAV-S: A versatile capsid variant for transduction of mouse and primate inner ear36
Enhancing Chimeric Antigen Receptor T Cell Anti-tumor Function through Advanced Media Design36
Modified mRNA-LNP Vaccines Confer Protection against Experimental DENV-2 Infection in Mice36
Superior Expansion and Cytotoxicity of Human Primary NK and CAR-NK Cells from Various Sources via Enriched Metabolic Pathways36
In Vivo Gene Editing of Muscle Stem Cells with Adeno-Associated Viral Vectors in a Mouse Model of Duchenne Muscular Dystrophy36
Development of a scalable and robust AEX method for enriched rAAV preparations in genome-containing VCs of serotypes 5, 6, 8, and 936
piggyBac system to co-express NKG2D CAR and IL-15 to augment the in vivo persistence and anti-AML activity of human peripheral blood NK cells35
Successful Preclinical Development of Gene Therapy for Recombinase-Activating Gene-1-Deficient SCID35
AAV-Genome Population Sequencing of Vectors Packaging CRISPR Components Reveals Design-Influenced Heterogeneity35
Mechanistic model for production of recombinant adeno-associated virus via triple transfection of HEK293 cells33
Anion-exchange HPLC assay for separation and quantification of empty and full capsids in multiple adeno-associated virus serotypes33
Timing of Intensive Immunosuppression Impacts Risk of Transgene Antibodies after AAV Gene Therapy in Nonhuman Primates32
Bone-Targeting AAV-Mediated Gene Silencing in Osteoclasts for Osteoporosis Therapy32
CRISPR-Cas9-Mediated In Vivo Gene Integration at the Albumin Locus Recovers Hemostasis in Neonatal and Adult Hemophilia B Mice32
Automated generation of gene-edited CAR T cells at clinical scale32
Allele-Specific Prevention of Nonsense-Mediated Decay in Cystic Fibrosis Using Homology-Independent Genome Editing32
iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation31
Overcoming Compensatory Mechanisms toward Chronic Drug Administration to Ensure Long-Term, Sustainable Beneficial Effects31
Targeting Antigen to the Surface of EVs Improves the In Vivo Immunogenicity of Human and Non-human Adenoviral Vaccines in Mice31
Empowering Retinal Gene Therapy with a Specific Promoter for Human Rod and Cone ON-Bipolar Cells31
A Single Intravenous Injection of AAV-PHP.B-hNDUFS4 Ameliorates the Phenotype of Ndufs4 Mice30
Quantitative analysis of genome packaging in recombinant AAV vectors by charge detection mass spectrometry29
Pharmacological interventions enhance virus-free generation of TRAC-replaced CAR T cells29
Mitigating Deficiencies in Evidence during Regulatory Assessments of Advanced Therapies: A Comparative Study with Other Biologicals29
Pooled Screens Identify GPR108 and TM9SF2 as Host Cell Factors Critical for AAV Transduction29
The impact of lentiviral vector genome size and producer cell genomic to gag-pol mRNA ratios on packaging efficiency and titre28
Characterization of AAV-Specific Affinity Ligands: Consequences for Vector Purification and Development Strategies28
Characterization of AAV-mediated dorsal root ganglionopathy28
Transplantation of miPSC/mESC-derived retinal ganglion cells into healthy and glaucomatous retinas28
Exosomes and organ-specific metastasis28
CERE-120 Prevents Irradiation-Induced Hypofunction and Restores Immune Homeostasis in Porcine Salivary Glands27
Nanoparticles versus Dendritic Cells as Vehicles to Deliver mRNA Encoding Multiple Epitopes for Immunotherapy27
Optimized Assessment of qPCR-Based Vector Copy Numbers as a Safety Parameter for GMP-Grade CAR T Cells and Monitoring of Frequency in Patients27
Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease26
Optimization of 5′ Untranslated Region of Modified mRNA for Use in Cardiac or Hepatic Ischemic Injury26
Clinical Development of Gene Therapies: The First Three Decades and Counting26
Adipose Mesenchymal Cells-Derived EVs Alleviate DOCA-Salt-Induced Hypertension by Promoting Cardio-Renal Protection26
Attenuation of Heparan Sulfate Proteoglycan Binding Enhances In Vivo Transduction of Human Primary Hepatocytes with AAV226
Human Mesenchymal Stem Cell Secretome Exhibits a Neuroprotective Effect over In Vitro Retinal Photoreceptor Degeneration26
In vivo PCSK9 gene editing using an all-in-one self-cleavage AAV-CRISPR system26
Efficient CRISPR-Cas9-based genome editing of β-globin gene on erythroid cells from homozygous β039-thalassemia patients26
Hair Cell Transduction Efficiency of Single- and Dual-AAV Serotypes in Adult Murine Cochleae25
Cas9 protein delivery non-integrating lentiviral vectors for gene correction in sickle cell disease25
Testing preexisting antibodies prior to AAV gene transfer therapy: rationale, lessons and future considerations25
Rosuvastatin Enhances VSV-G Lentiviral Transduction of NK Cells via Upregulation of the Low-Density Lipoprotein Receptor25
A flexible, thermostable nanostructured lipid carrier platform for RNA vaccine delivery25
AAV2/6 Gene Therapy in a Murine Model of Fabry Disease Results in Supraphysiological Enzyme Activity and Effective Substrate Reduction25
Manufacturing Dendritic Cells for Immunotherapy: Monocyte Enrichment24
Purification of Human CD34+CD90+ HSCs Reduces Target Cell Population and Improves Lentiviral Transduction for Gene Therapy24
Adeno-associated virus serotype 9 antibodies in patients screened for treatment with onasemnogene abeparvovec24
Enzyme Replacement Therapy Can Reverse Pathogenic Cascade in Pompe Disease24
High Frequency Production of T Cell-Derived iPSC Clones Capable of Generating Potent Cytotoxic T Cells24
Enriching leukapheresis improves T cell activation and transduction efficiency during CAR T processing23
Translational Feasibility of Lumbar Puncture for Intrathecal AAV Administration23
Characteristics of the Coronavirus Disease 2019 and related Therapeutic Options23
Targeted epigenetic repression by CRISPR/dSaCas9 suppresses pathogenic DUX4-fl expression in FSHD23
Systemic and local immune responses to intraocular AAV vector administration in non-human primates23
Factors Impacting Efficacy of AAV-Mediated CRISPR-Based Genome Editing for Treatment of Choroidal Neovascularization23
Rapid Lentiviral Vector Producer Cell Line Generation Using a Single DNA Construct23
Comparison of AAV-Mediated Optogenetic Vision Restoration between Retinal Ganglion Cell Expression and ON Bipolar Cell Targeting22
Chemically Defined, High-Density Insect Cell-Based Expression System for Scalable AAV Vector Production22
Metformin, an AMPK Activator, Inhibits Activation of FLSs but Promotes HAPLN1 Secretion22
Simple and Fast SEC-Based Protocol to Isolate Human Plasma-Derived Extracellular Vesicles for Transcriptional Research22
Impact of intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II22
Evaluating the Potential of T Cell Receptor Repertoires in Predicting the Prognosis of Resectable Non-Small Cell Lung Cancers22
Soluble Klotho Improves Hepatic Glucose and Lipid Homeostasis in Type 2 Diabetes22
Applying machine learning to predict viral assembly for adeno-associated virus capsid libraries22
Lentiviral Vector Production Titer Is Not Limited in HEK293T by Induced Intracellular Innate Immunity22
Rapid Transduction and Expansion of Transduced T Cells with Maintenance of Central Memory Populations22
Induction of ER Stress by an AAV5 BDD FVIII Construct Is Dependent on the Strength of the Hepatic-Specific Promoter21
Site-Directed Mutagenesis Improves the Transduction Efficiency of Capsid Library-Derived Recombinant AAV Vectors21
Cell therapy with hiPSC-derived RPE cells and RPCs prevents visual function loss in a rat model of retinal degeneration21
iMATCH: an integrated modular assembly system for therapeutic combination high-capacity adenovirus gene therapy21
Cerebral Organoids: A Human Model for AAV Capsid Selection and Therapeutic Transgene Efficacy in the Brain21
Multiplex CRISPR/Cas9 genome editing in hematopoietic stem cells for fetal hemoglobin reinduction generates chromosomal translocations21
Assessment of genome packaging in AAVs using Orbitrap-based charge-detection mass spectrometry21
Cross-Packaging and Capsid Mosaic Formation in Multiplexed AAV Libraries21
CRISPR-Cas9 Gene Editing of Hematopoietic Stem Cells from Patients with Friedreich’s Ataxia21
In vivo overexpression of frataxin causes toxicity mediated by iron-sulfur cluster deficiency21
Low incidence of hepatocellular carcinoma in mice and cats treated with systemic adeno-associated viral vectors21
High-Resolution Histological Landscape of AAV DNA Distribution in Cellular Compartments and Tissues following Local and Systemic Injection21
A Single “All-in-One” Helper-Dependent Adenovirus to Deliver Donor DNA and CRISPR/Cas9 for Efficient Homology-Directed Repair20
Monolayer platform using human biopsy-derived duodenal organoids for pharmaceutical research20
Promoter usage regulating the surface density of CAR molecules may modulate the kinetics of CAR-T cells in vivo20
AAV6 Vexosomes Mediate Robust Suicide Gene Delivery in a Murine Model of Hepatocellular Carcinoma20
Current landscape of clinical development and approval of advanced therapies20
Antigen modifications improve nucleoside-modified mRNA-based influenza virus vaccines in mice20
CAR T Cell Generation by piggyBac Transposition from Linear Doggybone DNA Vectors Requires Transposon DNA-Flanking Regions20
Nanoplasmid Vectors Co-expressing Innate Immune Agonists Enhance DNA Vaccines for Venezuelan Equine Encephalitis Virus and Ebola Virus20
Improved diabetic wound healing by LFcinB is associated with relevant changes in the skin immune response and microbiota20
rAAV2-Retro Enables Extensive and High-Efficient Transduction of Lower Motor Neurons following Intramuscular Injection20
Preclinical biodistribution, tropism, and efficacy of oligotropic AAV/Olig001 in a mouse model of congenital white matter disease20
Inhibition of KDM1A activity restores adult neurogenesis and improves hippocampal memory in a mouse model of Kabuki syndrome20
Safety and efficacy of an engineered hepatotropic AAV gene therapy for ornithine transcarbamylase deficiency in cynomolgus monkeys20
Circulating miR-4763-3p Is a Novel Potential Biomarker Candidate for Human Adult Fulminant Myocarditis20
Reversing Acute Kidney Injury Using Pulsed Focused Ultrasound and MSC Therapy: A Role for HSP-Mediated PI3K/AKT Signaling19
Biodistribution of intravitreal lenadogene nolparvovec gene therapy in nonhuman primates19
Assessing production variability in empty and filled adeno-associated viruses by single molecule mass analyses19
Generation of hypoimmunogenic induced pluripotent stem cells by CRISPR-Cas9 system and detailed evaluation for clinical application19
Effective Multi-lineage Engraftment in a Mouse Model of Fanconi Anemia Using Non-genotoxic Antibody-Based Conditioning19
Pre-clinical dose-escalation studies establish a therapeutic range for U7snRNA-mediated DMD exon 2 skipping19
AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice and Achieves Widespread Distribution of SGSH in Large Animal Brains19
Molecular subtyping and functional validation of TTK, TPX2, UBE2C, and LRP8 in sensitivity of TNBC to paclitaxel19
Safe and efficient in vivo hematopoietic stem cell transduction in nonhuman primates using HDAd5/35++ vectors19
Experimental Variables that Affect Human Hepatocyte AAV Transduction in Liver Chimeric Mice19
A consolidated AAV system for single-cut CRISPR correction of a common Duchenne muscular dystrophy mutation19
In Vitro and In Vivo Amenability to Migalastat in Fabry Disease18
CRISPAltRations: A validated cloud-based approach for interrogation of double-strand break repair mediated by CRISPR genome editing18
Gene therapy strategies for idiopathic pulmonary fibrosis: recent advances, current challenges, and future directions18
Liver-Directed but Not Muscle-Directed AAV-Antibody Gene Transfer Limits Humoral Immune Responses in Rhesus Monkeys18
A Long Intergenic Non-coding RNA, LINC01426, Promotes Cancer Progression via AZGP1 and Predicts Poor Prognosis in Patients with LUAD18
Advances and challenges in adeno-associated viral inner-ear gene therapy for sensorineural hearing loss18
Lentiviral Vector Production from a Stable Packaging Cell Line Using a Packed Bed Bioreactor18
Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity18
Engineering and In Vitro Selection of a Novel AAV3B Variant with High Hepatocyte Tropism and Reduced Seroreactivity18
Enhanced Inner-Ear Organoid Formation from Mouse Embryonic Stem Cells by Photobiomodulation18
CRISPR-Cpf1 Activation of Endogenous BMP4 Gene for Osteogenic Differentiation of Umbilical-Cord-Derived Mesenchymal Stem Cells18
Novel human liver-tropic AAV variants define transferable domains that markedly enhance the human tropism of AAV7 and AAV817
A hierarchical and collaborative BRD4/CEBPD partnership governs vascular smooth muscle cell inflammation17
Immunogenicity assessment of AAV-based gene therapies: An IQ consortium industry white paper17
Wound Healing Properties of Histatin-5 and Identification of a Functional Domain Required for Histatin-5-Induced Cell Migration17
Laboratory-Scale Lentiviral Vector Production and Purification for Enhanced Ex Vivo and In Vivo Genetic Engineering17
Implications of circulating neurofilaments for spinal muscular atrophy treatment early in life: A case series17
ImmTOR nanoparticles enhance AAV transgene expression after initial and repeat dosing in a mouse model of methylmalonic acidemia17
ISPD Overexpression Enhances Ribitol-Induced Glycosylation of α-Dystroglycan in Dystrophic FKRP Mutant Mice17
Skeletal Muscle Is an Antigen Reservoir in Integrase-Defective Lentiviral Vector-Induced Long-Term Immunity17
Engineered extracellular vesicles directed to the spike protein inhibit SARS-CoV-217
Comprehensive and systemic optimization for improving the yield of SARS-CoV-2 spike pseudotyped virus17
Germline CRISPR/Cas9-Mediated Gene Editing Prevents Vision Loss in a Novel Mouse Model of Aniridia17
A qPCR Method for AAV Genome Titer with ddPCR-Level of Accuracy and Precision17
Liver-Targeted AAV8 Gene Therapy Ameliorates Skeletal and Cardiovascular Pathology in a Mucopolysaccharidosis IVA Murine Model17
High throughput screening of novel AAV capsids identifies variants for transduction of adult NSCs within the subventricular zone16
Development and Optimization of a Hydrophobic Interaction Chromatography-Based Method of AAV Harvest, Capture, and Recovery16
Intralingual and Intrapleural AAV Gene Therapy Prolongs Survival in a SOD1 ALS Mouse Model16
Characterizing the cellular immune response to subretinal AAV gene therapy in the murine retina16
Structural basis for the neurotropic AAV9 and the engineered AAVPHP.eB recognition with cellular receptors16
Long-Term Efficacy of AAV9-U7snRNA-Mediated Exon 51 Skipping in mdx52 Mice16
Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH16
Analysis of Aflibercept Expression in NHPs following Intravitreal Administration of ADVM-022, a Potential Gene Therapy for nAMD16
Modulating immune responses to AAV by expanded polyclonal T-regs and capsid specific chimeric antigen receptor T-regulatory cells16
Generation of Nonhuman Primate Model of Cone Dysfunction through In Situ AAV-Mediated CNGB3 Ablation16
Adipose Tissue: An Emerging Target for Adeno-associated Viral Vectors16
Non-toxic HSC Transplantation-Based Macrophage/Microglia-Mediated GDNF Delivery for Parkinson’s Disease16
Seven-year follow-up of durability and safety of AAV CNS gene therapy for a lysosomal storage disorder in a large animal16
Treatment of Hypertensive Heart Disease by Targeting Smad3 Signaling in Mice16
Systematic improvements in lentiviral transduction of primary human natural killer cells undergoing ex vivo expansion16
Optimization of AAV6 transduction enhances site-specific genome editing of primary human lymphocytes16
Human iPSC-Derived Neural Crest Stem Cells Exhibit Low Immunogenicity15
A pro-inflammatory mediator USP11 enhances the stability of p53 and inhibits KLF2 in intracerebral hemorrhage15
NFAT-Specific Inhibition by dNP2-VIVIT Ameliorates Autoimmune Encephalomyelitis by Regulation of Th1 and Th1715
In Situ Detection of Adeno-associated Viral Vector Genomes with SABER-FISH15
Vector Copy Distribution at a Single-Cell Level Enhances Analytical Characterization of Gene-Modified Cell Therapies15
7T MRI Predicts Amelioration of Neurodegeneration in the Brain after AAV Gene Therapy15
HIV-Specific T Cells Can Be Generated against Non-escaped T Cell Epitopes with a GMP-Compliant Manufacturing Platform15
Circulating neurofilament light chain as a promising biomarker of AAV-induced dorsal root ganglia toxicity in nonclinical toxicology species15
Rapid Delivery of Nanobodies/VHHs into Living Cells via Expressing In Vitro-Transcribed mRNA15
Manufacturing NKG2D CAR-T cells with piggyBac transposon vectors and K562 artificial antigen-presenting cells15
A Rapid and Sensitive Nucleic Acid Amplification Technique for Mycoplasma Screening of Cell Therapy Products15
Efficient In Utero Gene Transfer to the Mammalian Inner Ears by the Synthetic Adeno-Associated Viral Vector Anc80L6515
Directed Evolution of AAV Serotype 5 for Increased Hepatocyte Transduction and Retained Low Humoral Seroreactivity15
Molecular analysis of AAV5-hFVIII-SQ vector-genome-processing kinetics in transduced mouse and nonhuman primate livers15
Novel GAA Variants and Mosaicism in Pompe Disease Identified by Extended Analyses of Patients with an Incomplete DNA Diagnosis15
Autologous antigen-presenting cells efficiently expand piggyBac transposon CAR-T cells with predominant memory phenotype15
A DNA Vaccine That Encodes an Antigen-Presenting Cell-Specific Heterodimeric Protein Protects against Cancer and Influenza14
Gene Therapy Preserves Retinal Structure and Function in a Mouse Model of NMNAT1-Associated Retinal Degeneration14
Depletion of high-content CD14+ cells from apheresis products is critical for successful transduction and expansion of CAR T cells during large-scale cGMP manufacturing14
Design and Testing of Vector-Producing HEK293T Cells Bearing a Genomic Deletion of the SV40 T Antigen Coding Region14
Systemic delivery of an AAV9 exon-skipping vector significantly improves or prevents features of Duchenne muscular dystrophy in the Dup2 mouse14
DNA Barcoding in Nonhuman Primates Reveals Important Limitations in Retrovirus Integration Site Analysis14
Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation14
CRISPR-Mediated Base Conversion Allows Discriminatory Depletion of Endogenous T Cell Receptors for Enhanced Synthetic Immunity14
Small Alphaherpesvirus Latency-Associated Promoters Drive Efficient and Long-Term Transgene Expression in the CNS14
Novel Non-integrating DNA Nano-S/MAR Vectors Restore Gene Function in Isogenic Patient-Derived Pancreatic Tumor Models14
Combined Treatment with Peptide-Conjugated Phosphorodiamidate Morpholino Oligomer-PPMO and AAV-U7 Rescues the Severe DMD Phenotype in Mice14
Applying a clinical lens to animal models of CAR-T cell therapies14
C3 Transferase-Expressing scAAV2 Transduces Ocular Anterior Segment Tissues and Lowers Intraocular Pressure in Mouse and Monkey14
Visceral adipose tissue-directed FGF21 gene therapy improves metabolic and immune health in BTBR mice14
Point Mutations in Retargeted gD Eliminate the Sensitivity of EGFR/EGFRvIII-Targeted HSV to Key Neutralizing Antibodies14
rAAV8 and rAAV9-Mediated Long-Term Muscle Transduction with Tacrolimus (FK506) in Non-Human Primates14
Establishment of SLC15A1/PEPT1-Knockout Human-Induced Pluripotent Stem Cell Line for Intestinal Drug Absorption Studies14
Discovery of key genes as novel biomarkers specifically associated with HPV-negative cervical cancer14
MTA1, a Target of Resveratrol, Promotes Epithelial-Mesenchymal Transition of Endometriosis via ZEB214
Immunoresponse to Gene-Modified Hematopoietic Stem Cells14
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