Statistics in Medicine

Papers
(The median citation count of Statistics in Medicine is 1. The table below lists those papers that are above that threshold based on CrossRef citation counts [max. 250 papers]. The publications cover those that have been published in the past four years, i.e., from 2021-02-01 to 2025-02-01.)
ArticleCitations
Joint modeling of association networks and longitudinal biomarkers: An application to childhood obesity300
Bayesian response adaptive randomization design with a composite endpoint of mortality and morbidity164
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Models for cluster randomized designs using ranked set sampling45
Improving the Effectiveness of Sample Size Re‐Estimation: An Operating Characteristic Focused, Hybrid Frequentist‐Bayesian Approach41
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Nonparametric estimation of marked survival data in the presence of dependent censoring41
Bayesian Borrowing With Multiple Heterogeneous Historical Studies Using Order Restricted Normalized Power Prior40
Hierarchical Multi‐Label Classification With Gene‐Environment Interactions in Disease Modeling35
Classification of disease recurrence using transition likelihoods with expectation‐maximization algorithm33
Bayesian network mediation analysis with application to the brain functional connectome33
Capturing the pool dilution effect in group testing regression: A Bayesian approach31
Adaptive response‐dependent two‐phase designs: Some results on robustness and efficiency31
Point estimation for adaptive trial designs I: A methodological review30
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SIM 40th Anniversary25
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Individualized empirical null estimation for exact tests of healthcare quality23
Comparing and combining data from immune assays based on left‐censored multivariate normal model assuming common assay differences across settings23
Approximate balancing weights for clustered observational study designs23
Robust rank‐based meta‐analyses for two‐sample designs with application to platelet counts of malaria infection data22
On the role of statisticians and modelers in responding to AIDS and COVID‐1922
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Overall assessment for selected markers from high‐throughput data22
Real time monitoring and prediction of time to endpoint maturation in clinical trials21
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Proportional likelihood ratio mixed model for discrete longitudinal data20
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Best practices in statistical computing19
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Enhancing long‐term survival prediction with two short‐term events: Landmarking with a flexible varying coefficient model18
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Flexible parametrization of graph‐theoretical features from individual‐specific networks for prediction18
Likelihood ratio combination of multiple biomarkers via smoothing spline estimated densities18
A Bayesian approach for estimating typhoid fever incidence from large‐scale facility‐based passive surveillance data17
Estimands for factorial trials16
A novel approach to assess dynamic treatment regimes embedded in a SMART with an ordinal outcome16
A semi‐parametric Bayesian model for semi‐continuous longitudinal data16
Deep causal feature extraction and inference with neuroimaging genetic data16
Evaluating effectiveness of public health intervention strategies for mitigating COVID‐19 pandemic16
Training and capacity building in medical statistics in Sub‐Saharan Africa: Impact of the London School of Hygiene & Tropical Medicine MSc in Medical Statistics, 1969 to 202116
Modeling the multi‐state natural history of rare diseases with heterogeneous individual patient data: A simulation study16
Sample size considerations for assessing treatment effect heterogeneity in randomized trials with heterogeneous intracluster correlations and variances15
The scale transformed power prior for use with historical data from a different outcome model15
Approximate Bayesian computation for the natural history of breast cancer, with application to data from a Milan cohort study15
Discussion on “Is group testing ready for prime‐time in disease identification”15
Mixture of longitudinal factor analyzers and their application to the assessment of chronic pain15
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Designing a longitudinal clinical trial based on a composite endpoint: Sample size, monitoring, and adaptation14
Synthesizing studies for comparing different treatment sequences in clinical trials14
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Kernel density estimation in mixture models with known mixture proportions13
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Use of likelihood estimates for variances for the design and evaluation of multiregional clinical trials with heterogeneous variances13
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Nonparametric bounds in two‐sample summary‐data Mendelian randomization: Some cautionary tales for practice12
Sample size formula for a win ratio endpoint12
A semiparametric Gumbel regression model for analyzing longitudinal data with non‐normal tails12
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A longitudinal transition imputation model for categorical data applied to a large registry dataset12
Event‐specific win ratios for inference with terminal and non‐terminal events12
Robust group variable screening based on maximum Lq‐likelihood estimation12
Similarity of competing risks models with constant intensities in an application to clinical healthcare pathways involving prostate cancer surgery12
Penalized likelihood estimation of a mixture cure Cox model with partly interval censoring—An application to thin melanoma12
When should matching be used in the design of cluster randomized trials?12
Prediction‐driven pooled testing methods: Application to HIV treatment monitoring in Rakai, Uganda11
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Statistical modeling of diabetic neuropathy: Exploring the dynamics of nerve mortality11
Estimating adjusted risk differences by multiply‐imputing missing control binary potential outcomes following propensity score‐matching11
Robust estimation and variable selection for the accelerated failure time model11
Point estimation, confidence intervals, and P‐values for optimal adaptive two‐stage designs with normal endpoints11
Restricted sub‐tree learning to estimate an optimal dynamic treatment regime using observational data11
Shared decision making of burdensome surveillance tests using personalized schedules and their burden and benefit11
An extended Bayesian semi‐mechanistic dose‐finding design for phase I oncology trials using pharmacokinetic and pharmacodynamic information10
Semiparametric linear transformation models for indirectly observed outcomes10
Variable selection in semiparametric regression models for longitudinal data with informative observation times10
Sample size calculation in hierarchical 2×2 factorial trials with unequal cluster sizes10
Uncertainty in lung cancer stage for survival estimation via set‐valued classification10
Estimation of non‐monotonic transition rates in a semi‐Markov process with covariates adjustments and application to caregivers' stress data10
Combining Mendelian randomization with the sibling comparison design10
Analyzing cohort studies with interval‐censored data: A new model‐based linear rank‐type test10
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Improving large‐scale estimation and inference for profiling health care providers10
Bayesian federated inference for estimating statistical models based on non‐shared multicenter data sets10
Double robust estimation of optimal partially adaptive treatment strategies: An application to breast cancer treatment using hormonal therapy10
Handling parametric assumptions in principal causal effect estimation using Gaussian mixtures10
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Estimation of vaccine efficacy for variants that emerge after the placebo group is vaccinated10
Unified estimation for Cox regression model with nonmonotone missing at random covariates10
Issues with the expected information matrix of linear mixed models provided by popular statistical packages under missingness at random dropout10
Inference about ratios of age‐standardized rates with sampling errors in the population denominators for estimating both rates10
Incorporating the dilution effect in group testing regression10
Balancing versus modelling in weighted analysis of non‐randomised studies with survival outcomes: A simulation study9
Comparing two hazard curves when there is a treatment time‐lag effect9
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Sensitivity analysis for principal ignorability violation in estimating complier and noncomplier average causal effects9
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Maximum approximate likelihood estimation in accelerated failure time model for interval‐censored data9
Network and covariate adjusted response‐adaptive design for binary response9
An enhanced cross‐sectional HIV incidence estimator that incorporates prior HIV test results9
Bayesian mixture modelling with ranked set samples9
A two‐level copula joint model for joint analysis of longitudinal and competing risks data9
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Optimal confidence intervals for the relative risk and odds ratio8
Bayesian additive regression trees for multivariate skewed responses8
Selection of number of clusters and warping penalty in clustering functional electrocardiogram8
Practical implementation of the partial ordering continual reassessment method in a Phase I combination‐schedule dose‐finding trial8
Unsupervised learning for medical data: A review of probabilistic factorization methods8
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Bayesian model‐averaged meta‐analysis in medicine8
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Two‐stage randomized clinical trials with a right‐censored endpoint: Comparison of frequentist and Bayesian adaptive designs8
Clayton copula for survival data with dependent censoring: An application to a tuberculosis treatment adherence data8
Semiparametric estimation of restricted mean survival time as a function of restriction time8
Letter to the editor: The use of fast approximate random forests using subsampling (rfsrc.fast) does not support the conclusion on sample sizes needed for random survival forests8
Vaccine adverse event enrichment tests8
Sample size adaptation designs and efficiency comparison with group sequential designs8
A simulation study of disaggregation regression for spatial disease mapping8
A flexible class of generalized joint frailty models for the analysis of survival endpoints8
The spike‐and‐slab quantile LASSO for robust variable selection in cancer genomics studies8
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Bayesian hierarchical profile regression for binary covariates8
An approximate quasi‐likelihood approach for error‐prone failure time outcomes and exposures8
A novel test by combining the maximum and minimum values among a large number of dependent Z‐scores with application to genome wide association study8
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On the parameter estimation of Box‐Cox transformation cure model7
Bayesian network meta‐regression hierarchical models using heavy‐tailed multivariate random effects with covariate‐dependent variances7
Use of win time for ordered composite endpoints in clinical trials7
Modeling multiple correlated end‐organ disease trajectories: A tutorial for multistate and joint models with applications in diabetes complications7
Spatial modeling of epidermal nerve fiber patterns7
Cluster randomized trial designs for modeling time‐varying intervention effects7
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Comparative poisson clinical trials of multiple experimental treatments vs a single control using the negative multinomial distribution7
Point estimation for adaptive trial designs II: Practical considerations and guidance7
A simplified stochastic EM algorithm for cure rate model with negative binomial competing risks: An application to breast cancer data7
Exact inference for fixed effects meta‐analysis of 2×2$$ 2\times 2 $$ tables7
Sample size calculation for randomized selection trials with a time‐to‐event endpoint and a margin of practical equivalence7
Are the tests overpowered or underpowered? A unified solution to correctly specify type I errors in design of clinical trials for two sample proportions7
G‐formula for observational studies under stratified interference, with application to bed net use on malaria7
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Semiparametric multivariate joint model for skewed‐longitudinal and survival data: A Bayesian approach7
A ROC‐based test for evaluating the group difference with an application to neonatal audiology screening7
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Bayesian transformation models with partly interval‐censored data7
Quantifying the feasibility of shortening clinical trial duration using surrogate markers7
Regression analysis of arbitrarily censored survival data under the proportional odds model7
Tracking the transmission dynamics of COVID‐19 with a time‐varying coefficient state‐space model7
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Parametric and nonparametric improvements in Bland and Altman's assessment of agreement method7
Conditional power and friends: The why and how of (un)planned, unblinded sample size recalculations in confirmatory trials7
Bayesian record linkage with variables in one file7
Semiparametric regression analysis of clustered interval‐censored failure time data with a cured subgroup7
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Estimation of standard deviations and inverse‐variance weights from an observed range7
New late‐emphasis and combination tests based on infimum and supremum logrank statistics with application in oncology trials7
RMST‐based multiple contrast tests in general factorial designs6
Inferring latent heterogeneity using many feature variables supervised by survival outcome6
Selection of within‐run quality control rules for laboratory biomarkers6
Exact test and exact confidence interval for the Cox model6
An augmented illness‐death model for semi‐competing risks with clinically immediate terminal events6
Bayesian spatial models for voxel‐wise prostate cancer classification using multi‐parametric magnetic resonance imaging data6
A Bayesian nonparametric approach to dynamic item‐response modeling: An application to the GUSTO cohort study6
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Categorisation of continuous covariates for stratified randomisation: How should we adjust?6
Gene‐gene interaction analysis incorporating network information via a structured Bayesian approach6
Integrative sparse partial least squares6
Optimal planning of adaptive two‐stage designs6
Towards robust and accurate estimates of the incubation time distribution, with focus on upper tail probabilities and SARS‐CoV‐2 infection6
Testing a global null hypothesis using ensemble machine learning methods6
Effective disease surveillance by using covariate information6
Introduction to computational causal inference using reproducible Stata, R, and Python code: A tutorial6
Dose finding studies for therapies with late‐onset toxicities: A comparison study of designs6
Meta‐analysis methods for multiple related markers: Applications to microbiome studies with the results on multiple α‐diversity indices6
Noninferiority testing with censoring when the event rate is low6
Multi‐state network meta‐analysis of progression and survival data6
Confidence interval estimation for treatment effects in cluster randomization trials based on ranks6
Multiparameter one‐sided tests for nonlinear mixed effects models with censored responses6
Constrained randomization and statistical inference for multi‐arm parallel cluster randomized controlled trials6
Dynamic path analysis for exploring treatment effect mediation processes in clinical trials with time‐to‐event endpoints6
A mixture distribution approach for assessing genetic impact from twin study6
Robust approach for variable selection with high dimensional longitudinal data analysis6
Bayesian hierarchical models for high‐dimensional mediation analysis with coordinated selection of correlated mediators6
Functional Principal Component Analysis for Continuous Non‐Gaussian, Truncated, and Discrete Functional Data6
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Do machine learning methods lead to similar individualized treatment rules? A comparison study on real data6
Surveillance for endemic infectious disease outbreaks: Adaptive sampling using profile likelihood estimation6
Generalized additive models to analyze nonlinear trends in biomedical longitudinal data using R: Beyond repeated measures ANOVA and linear mixed models5
Reclaiming independence in spatial‐clustering datasets: A series of data‐driven spatial weights matrices5
Investigation of patient‐sharing networks using a Bayesian network model selection approach for congruence class models5
Target estimands for efficient decision making: Response to comments on “Assessing the performance of population adjustment methods for anchored indirect comparisons: A simulation study”5
Sequential modeling for a class of reference‐based imputation methods in clinical trials with quantitative or binary outcomes5
Effect modification in anchored indirect treatment comparison: Comments on “Matching‐adjusted indirect comparisons: Application to time‐to‐event data”5
Laplacian‐P‐splines for Bayesian inference in the mixture cure model5
SpiderLearner: An ensemble approach to Gaussian graphical model estimation5
Dual‐agent dose‐finding in Phase I clinical trial—An extension of rapid enrollment design5
Prior elicitation for Gaussian spatial process: An application to TMS brain mapping5
Confidence sets for a level set in linear regression5
A Bayesian phase I/II platform design for co‐developing drug combination therapies for multiple indications5
A simulation‐extrapolation approach for regression analysis of misclassified current status data with the additive hazards model5
Measuring association among censored antibody titer data5
Propensity score methods for observational studies with clustered data: A review5
Comparisons of statistical methods for handling attrition in a follow‐up visit with complex survey sampling5
Improving main analysis by borrowing information from auxiliary data5
Estimands in heath technology assessment: a causal inference perspective5
Robustness of κ‐type coefficients for clinical agreement5
Evaluating joint confidence region of hypervolume under ROC manifold and generalized Youden index5
Group sequential multi‐arm multi‐stage trial design with treatment selection5
Two‐stage targeted maximum likelihood estimation for mixed aggregate and individual participant data analysis with an application to multidrug resistant tuberculosis5
Comparison of treatments with ordinal responses in trials with sequential monitoring and response‐adaptive randomization5
Predictive generalized varying‐coefficient longitudinal model5
Using instruments for selection to adjust for selection bias in Mendelian randomization5
Bayesian analysis for partly linear Cox model with measurement error and time‐varying covariate effect5
On information fraction for Fleming‐Harrington type weighted log‐rank tests in a group‐sequential clinical trial design5
CAPITAL: Optimal subgroup identification via constrained policy tree search5
Predictive signature development based on maximizing the area between receiver operating characteristic curves5
A tutorial on individualized treatment effect prediction from randomized trials with a binary endpoint5
Pitfalls of the concordance index for survival outcomes5
Comments on the debate between marginal and conditional estimands5
Assessing reproducibility of high‐throughput experiments in the case of missing data5
A comparison of bias‐adjusted generalized estimating equations for sparse binary data in small‐sample longitudinal studies5
Bayesian workflow for disease transmission modeling in Stan5
Testing for an ignorable sampling bias under random double truncation5
The polytomous discrimination index for prediction involving multistate processes under intermittent observation5
A comparison of hyperparameter tuning procedures for clinical prediction models: A simulation study5
Transportability of model‐based estimands in evidence synthesis5
A puzzle of proportions: Two popular Bayesian tests can yield dramatically different conclusions5
Minimum sample size calculations for external validation of a clinical prediction model with a time‐to‐event outcome5
Comments on “Sample size formula for a win ratio endpoint” by R. X. Yu and J. Ganju4
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Studentized permutation method for comparing two restricted mean survival times with small sample from randomized trials4
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Sample size formula for a win ratio endpoint4
Accounting for selection bias due to death in estimating the effect of wealth shock on cognition for the Health and Retirement Study4
A robust Bayesian bias‐adjusted random effects model for consideration of uncertainty about bias terms in evidence synthesis4
How vague is vague? How informative is informative? Reference analysis for Bayesian meta‐analysis4
A two‐way flexible generalized gamma transformation cure rate model4
Comparison of combination methods to create calibrated ensemble forecasts for seasonal influenza in the U.S.4
Modeling multivariate age‐related imaging variables with dependencies4
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