Statistics in Medicine

Article	Citations
Joint modeling of association networks and longitudinal biomarkers: An application to childhood obesity	352
Bayesian response adaptive randomization design with a composite endpoint of mortality and morbidity	199
Issue Information	124
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Models for cluster randomized designs using ranked set sampling	64
Nonparametric estimation of marked survival data in the presence of dependent censoring	51
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Classification of disease recurrence using transition likelihoods with expectation‐maximization algorithm	48
Adaptive response‐dependent two‐phase designs: Some results on robustness and efficiency	47
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Restricted sub‐tree learning to estimate an optimal dynamic treatment regime using observational data	42
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SIM 40th Anniversary	37
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Individualized empirical null estimation for exact tests of healthcare quality	34
Approximate balancing weights for clustered observational study designs	34
Designing a longitudinal clinical trial based on a composite endpoint: Sample size, monitoring, and adaptation	33
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Synthesizing studies for comparing different treatment sequences in clinical trials	31
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Kernel density estimation in mixture models with known mixture proportions	26

Use of likelihood estimates for variances for the design and evaluation of multiregional clinical trials with heterogeneous variances	26
Nonparametric bounds in two‐sample summary‐data Mendelian randomization: Some cautionary tales for practice	25
Penalized likelihood estimation of a mixture cure Cox model with partly interval censoring—An application to thin melanoma	25
CORRECTION	25
Event‐specific win ratios for inference with terminal and non‐terminal events	24
Robust group variable screening based on maximum Lq‐likelihood estimation	24
A longitudinal transition imputation model for categorical data applied to a large registry dataset	24
Comparing and combining data from immune assays based on left‐censored multivariate normal model assuming common assay differences across settings	23
Robust rank‐based meta‐analyses for two‐sample designs with application to platelet counts of malaria infection data	22
Overall assessment for selected markers from high‐throughput data	22
Issue Information	22
On the role of statisticians and modelers in responding to AIDS and COVID‐19	21
Real time monitoring and prediction of time to endpoint maturation in clinical trials	20
Semiparametric multivariate joint model for skewed‐longitudinal and survival data: A Bayesian approach	18
Semiparametric regression analysis of clustered interval‐censored failure time data with a cured subgroup	18
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Bayesian record linkage with variables in one file	17
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Deep causal feature extraction and inference with neuroimaging genetic data	16
Best practices in statistical computing	16
Likelihood ratio combination of multiple biomarkers via smoothing spline estimated densities	16
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Flexible parametrization of graph‐theoretical features from individual‐specific networks for prediction	16
Enhancing long‐term survival prediction with two short‐term events: Landmarking with a flexible varying coefficient model	16
A novel approach to assess dynamic treatment regimes embedded in a SMART with an ordinal outcome	15
Modeling the multi‐state natural history of rare diseases with heterogeneous individual patient data: A simulation study	15
Evaluating effectiveness of public health intervention strategies for mitigating COVID‐19 pandemic	15
Training and capacity building in medical statistics in Sub‐Saharan Africa: Impact of the London School of Hygiene & Tropical Medicine MSc in Medical Statistics, 1969 to 2021	14
Estimands for factorial trials	14
Discussion on “Is group testing ready for prime‐time in disease identification”	13
Mixture of longitudinal factor analyzers and their application to the assessment of chronic pain	13
Sample size considerations for assessing treatment effect heterogeneity in randomized trials with heterogeneous intracluster correlations and variances	13
The scale transformed power prior for use with historical data from a different outcome model	13
Approximate Bayesian computation for the natural history of breast cancer, with application to data from a Milan cohort study	13
A semi‐parametric Bayesian model for semi‐continuous longitudinal data	13
A semiparametric Gumbel regression model for analyzing longitudinal data with non‐normal tails	12
Point estimation, confidence intervals, and P‐values for optimal adaptive two‐stage designs with normal endpoints	12
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Estimating adjusted risk differences by multiply‐imputing missing control binary potential outcomes following propensity score‐matching	12
Statistical modeling of diabetic neuropathy: Exploring the dynamics of nerve mortality	12
Selection of within‐run quality control rules for laboratory biomarkers	12
Shared decision making of burdensome surveillance tests using personalized schedules and their burden and benefit	12
Prediction‐driven pooled testing methods: Application to HIV treatment monitoring in Rakai, Uganda	12
Handling parametric assumptions in principal causal effect estimation using Gaussian mixtures	11
Combining Mendelian randomization with the sibling comparison design	11
Estimation of vaccine efficacy for variants that emerge after the placebo group is vaccinated	11

Unified estimation for Cox regression model with nonmonotone missing at random covariates	11
Modeling multiple correlated end‐organ disease trajectories: A tutorial for multistate and joint models with applications in diabetes complications	11
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Variable selection in semiparametric regression models for longitudinal data with informative observation times	11
Conditional power and friends: The why and how of (un)planned, unblinded sample size recalculations in confirmatory trials	11
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An extended Bayesian semi‐mechanistic dose‐finding design for phase I oncology trials using pharmacokinetic and pharmacodynamic information	11
Analyzing cohort studies with interval‐censored data: A new model‐based linear rank‐type test	11
Uncertainty in lung cancer stage for survival estimation via set‐valued classification	11
G‐formula for observational studies under stratified interference, with application to bed net use on malaria	11
Estimation of non‐monotonic transition rates in a semi‐Markov process with covariates adjustments and application to caregivers' stress data	10
Bayesian federated inference for estimating statistical models based on non‐shared multicenter data sets	10
Bayesian mixture modelling with ranked set samples	10
Network and covariate adjusted response‐adaptive design for binary response	10
An enhanced cross‐sectional HIV incidence estimator that incorporates prior HIV test results	10
Issue Information	10
Issues with the expected information matrix of linear mixed models provided by popular statistical packages under missingness at random dropout	10
Inference about ratios of age‐standardized rates with sampling errors in the population denominators for estimating both rates	10
Balancing versus modelling in weighted analysis of non‐randomised studies with survival outcomes: A simulation study	10
Comparing two hazard curves when there is a treatment time‐lag effect	10
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Estimation of standard deviations and inverse‐variance weights from an observed range	10
Double robust estimation of optimal partially adaptive treatment strategies: An application to breast cancer treatment using hormonal therapy	10
Sample size calculation in hierarchical 2×2 factorial trials with unequal cluster sizes	10
Sensitivity analysis for principal ignorability violation in estimating complier and noncomplier average causal effects	10
A two‐level copula joint model for joint analysis of longitudinal and competing risks data	10
Maximum approximate likelihood estimation in accelerated failure time model for interval‐censored data	10
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Improving large‐scale estimation and inference for profiling health care providers	10
Issue Information	9
Selection of number of clusters and warping penalty in clustering functional electrocardiogram	9
Optimal confidence intervals for the relative risk and odds ratio	9
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Unsupervised learning for medical data: A review of probabilistic factorization methods	9
Clayton copula for survival data with dependent censoring: An application to a tuberculosis treatment adherence data	9
The spike‐and‐slab quantile LASSO for robust variable selection in cancer genomics studies	9
A flexible class of generalized joint frailty models for the analysis of survival endpoints	9
Letter to the editor: The use of fast approximate random forests using subsampling (rfsrc.fast) does not support the conclusion on sample sizes needed for random survival forests	9
Bayesian hierarchical profile regression for binary covariates	9
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Semiparametric estimation of restricted mean survival time as a function of restriction time	9
Bayesian additive regression trees for multivariate skewed responses	9
Two‐stage randomized clinical trials with a right‐censored endpoint: Comparison of frequentist and Bayesian adaptive designs	9
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Sequential modeling for a class of reference‐based imputation methods in clinical trials with quantitative or binary outcomes	8
Exact inference for fixed effects meta‐analysis of 2×2$$ 2\times 2 $$ tables	8
Bayesian network meta‐regression hierarchical models using heavy‐tailed multivariate random effects with covariate‐dependent variances	8
Spatial modeling of epidermal nerve fiber patterns	8
Vaccine adverse event enrichment tests	8
Sample size adaptation designs and efficiency comparison with group sequential designs	8
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Transporting experimental results with entropy balancing	8
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Bayesian transformation models with partly interval‐censored data	8
Are the tests overpowered or underpowered? A unified solution to correctly specify type I errors in design of clinical trials for two sample proportions	8
An approximate quasi‐likelihood approach for error‐prone failure time outcomes and exposures	8
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Two‐stage targeted maximum likelihood estimation for mixed aggregate and individual participant data analysis with an application to multidrug resistant tuberculosis	8
Constrained randomization and statistical inference for multi‐arm parallel cluster randomized controlled trials	8
Use of win time for ordered composite endpoints in clinical trials	8
Analysis of Longitudinal Lupus Data Using Multivariate t‐Linear Models	8
Sample size calculation for randomized selection trials with a time‐to‐event endpoint and a margin of practical equivalence	8
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Cluster randomized trial designs for modeling time‐varying intervention effects	8
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Point estimation for adaptive trial designs II: Practical considerations and guidance	7
Surveillance for endemic infectious disease outbreaks: Adaptive sampling using profile likelihood estimation	7
When should matching be used in the design of cluster randomized trials?	7
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Testing a global null hypothesis using ensemble machine learning methods	7
Do machine learning methods lead to similar individualized treatment rules? A comparison study on real data	7
A Bayesian nonparametric approach to dynamic item‐response modeling: An application to the GUSTO cohort study	7
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Quantifying the feasibility of shortening clinical trial duration using surrogate markers	7
Regression analysis of arbitrarily censored survival data under the proportional odds model	7
Bayesian model‐averaged meta‐analysis in medicine	7
Dose finding studies for therapies with late‐onset toxicities: A comparison study of designs	7

Gene‐gene interaction analysis incorporating network information via a structured Bayesian approach	7
A mixture distribution approach for assessing genetic impact from twin study	7
Towards robust and accurate estimates of the incubation time distribution, with focus on upper tail probabilities and SARS‐CoV‐2 infection	7
Multiparameter one‐sided tests for nonlinear mixed effects models with censored responses	7
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Categorisation of continuous covariates for stratified randomisation: How should we adjust?	7
On the parameter estimation of Box‐Cox transformation cure model	7
Tracking the transmission dynamics of COVID‐19 with a time‐varying coefficient state‐space model	7
New late‐emphasis and combination tests based on infimum and supremum logrank statistics with application in oncology trials	7
Bayesian hierarchical models for high‐dimensional mediation analysis with coordinated selection of correlated mediators	7
An augmented illness‐death model for semi‐competing risks with clinically immediate terminal events	7
Inferring latent heterogeneity using many feature variables supervised by survival outcome	7
Robust approach for variable selection with high dimensional longitudinal data analysis	7
Noninferiority testing with censoring when the event rate is low	7
Multi‐state network meta‐analysis of progression and survival data	7
Comparison of treatments with ordinal responses in trials with sequential monitoring and response‐adaptive randomization	6
Target estimands for population‐adjusted indirect comparisons	6
Correction to “Propensity score weighting for covariate adjustment in randomized clinical trials”	6
Measuring association among censored antibody titer data	6
Reclaiming independence in spatial‐clustering datasets: A series of data‐driven spatial weights matrices	6
SpiderLearner: An ensemble approach to Gaussian graphical model estimation	6
Effective disease surveillance by using covariate information	6
A ROC‐based test for evaluating the group difference with an application to neonatal audiology screening	6
Estimands in heath technology assessment: a causal inference perspective	6
Dual‐agent dose‐finding in Phase I clinical trial—An extension of rapid enrollment design	6
Propensity score methods for observational studies with clustered data: A review	6
Dynamic path analysis for exploring treatment effect mediation processes in clinical trials with time‐to‐event endpoints	6
A comparison of hyperparameter tuning procedures for clinical prediction models: A simulation study	6
Laplacian‐P‐splines for Bayesian inference in the mixture cure model	6
Bayesian Safety and Futility Monitoring in Phase II Trials Using One Utility‐Based Rule	6
Bayesian adaptive design for covariate‐adaptive historical control information borrowing	6
Incorporating survival data into case‐control studies with incident and prevalent cases	6
Predictive generalized varying‐coefficient longitudinal model	6
Testing for an ignorable sampling bias under random double truncation	6
The polytomous discrimination index for prediction involving multistate processes under intermittent observation	6
Comparisons of statistical methods for handling attrition in a follow‐up visit with complex survey sampling	6
Exact test and exact confidence interval for the Cox model	6
Comments on the debate between marginal and conditional estimands	6
Using instruments for selection to adjust for selection bias in Mendelian randomization	6
RMST‐based multiple contrast tests in general factorial designs	6
A puzzle of proportions: Two popular Bayesian tests can yield dramatically different conclusions	6
Group sequential multi‐arm multi‐stage trial design with treatment selection	6
Estimands and Cumulative Incidence Function Regression in Clinical Trials: Some New Results on Interpretability and Robustness	6
Target estimands for efficient decision making: Response to comments on “Assessing the performance of population adjustment methods for anchored indirect comparisons: A simulation study”	6
Predictive signature development based on maximizing the area between receiver operating characteristic curves	6
A comparison of bias‐adjusted generalized estimating equations for sparse binary data in small‐sample longitudinal studies	6
Bayesian analysis for partly linear Cox model with measurement error and time‐varying covariate effect	6
Prior elicitation for Gaussian spatial process: An application to TMS brain mapping	6
A simulation‐extrapolation approach for regression analysis of misclassified current status data with the additive hazards model	6
Confidence sets for a level set in linear regression	6
Effect modification in anchored indirect treatment comparison: Comments on “Matching‐adjusted indirect comparisons: Application to time‐to‐event data”	6
Transportability of model‐based estimands in evidence synthesis	6
Investigation of patient‐sharing networks using a Bayesian network model selection approach for congruence class models	6
A tutorial on individualized treatment effect prediction from randomized trials with a binary endpoint	5
Guidelines and Best Practices for the Use of Targeted Maximum Likelihood and Machine Learning When Estimating Causal Effects of Exposures on Time‐To‐Event Outcomes	5
Capturing the pool dilution effect in group testing regression: A Bayesian approach	5
Assessing reproducibility of high‐throughput experiments in the case of missing data	5
Improving main analysis by borrowing information from auxiliary data	5
Modelling Volume‐Outcome Relationships in Health Care	5
Correction to “DL 101: Basic Introduction to Deep Learning With Its Application in Biomedical Related Fields”	5
Estimating Average Treatment Effects With Support Vector Machines	5
Transformed ROC Curve for Biomarker Evaluation	5
Leveraging External Aggregated Information for the Marginal Accelerated Failure Time Model	5
Quantifying Overdiagnosis for Multicancer Detection Tests: A Novel Method	5
Bayesian workflow for disease transmission modeling in Stan	5
Point estimation for adaptive trial designs I: A methodological review	5
Overcoming Model Uncertainty — How Equivalence Tests Can Benefit From Model Averaging	5
Practical implementation of the partial ordering continual reassessment method in a Phase I combination‐schedule dose‐finding trial	5
Robustness of κ‐type coefficients for clinical agreement	5
Optimizing dynamic predictions from joint models using super learning	5
Bayesian network mediation analysis with application to the brain functional connectome	5
Skewness‐Corrected Confidence Intervals for Predictive Values in Enrichment Studies	5
Regression Approaches to Assess Effect of Treatments That Arrest Progression of Symptoms	5
Data fusion for predicting long‐term program impacts	5
Sequential Monitoring of Covariate‐Adaptive Randomized Clinical Trials With Non‐Parametric Approaches	5
Evaluating joint confidence region of hypervolume under ROC manifold and generalized Youden index	5
Preservation of Type I Error for Partially‐Unblinded Sample Size Re‐Estimation	5
Issue Information	5
CAPITAL: Optimal subgroup identification via constrained policy tree search	5
A Bayesian approach for estimating typhoid fever incidence from large‐scale facility‐based passive surveillance data	5
Estimating Mean Viral Load Trajectory From Intermittent Longitudinal Data and Unknown Time Origins	5
Random Survival Forest for Censored Functional Data	5
Nonparametric Biomarker Based Treatment Selection With Reproducibility Data	5
Estimating Time‐Varying Exposure Effects Through Continuous‐Time Modelling in Mendelian Randomization	5
Introduction to computational causal inference using reproducible Stata, R, and Python code: A tutorial	5
A simulation study of disaggregation regression for spatial disease mapping	5
Comments on “Sample size formula for a win ratio endpoint” by R. X. Yu and J. Ganju	4
A Bayesian approach to study design and analysis with type I error rate control for response variables of mixed types	4
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Sample size formula for a win ratio endpoint	4
Scalable algorithms for semiparametric accelerated failure time models in high dimensions	4
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Fractional accumulative calibration‐free odds (f‐aCFO) design for delayed toxicity in phase I clinical trials	4
Modeling multivariate age‐related imaging variables with dependencies	4